Ionis Pharmaceuticals (IONS) 09/06/2016 http://www.ionispharma.com/ Pipeline: Focus on developing treatment for rare and severe diseases. Their most important drug candidates are in this category. Very diverse and rich pipeline. Product Indication Status KYNAMRO Homozygous Familial Hypercholesterolemia (HoFH) Approved Alicaforsen Pouchitis Approved IONIS-TTRRx Familial Amyloid Polyneuropathy Phase 3 Nusinersen Infants and Children with Spinal Muscular Atrophy Phase 3 Volanesorsen Familial
http://www.ionispharma.com/ Pipeline: Focus on developing treatment for rare and severe diseases. Their most important drug candidates are in this category. Very diverse and rich pipeline. Product Indication Status KYNAMRO Homozygous Familial Hypercholesterolemia (HoFH) Approved Alicaforsen Pouchitis Approved IONIS-TTRRx Familial Amyloid Polyneuropathy Phase 3 Nusinersen Infants and Children with Spinal Muscular Atrophy Phase 3 Volanesorsen Familial